Title |
Long-term efficacy and safety of sapropterin in patients who initiated sapropterin at < 4 years of age with phenylketonuria: results of the 3-year extension of the SPARK open-label, multicentre, randomised phase IIIb trial |
|---|---|
Involved |
Ania Muntau (Verfasser)
Alberto Burlina (Verfasser) François Eyskens (Verfasser) Peter Freisinger (Verfasser)
Vincenzo Leuzzi (Verfasser)
Hatice Serap Sivri (Verfasser) Gwendolyn Gramer (Verfasser) Renata Pazdírková (Verfasser) Maureen Cleary (Verfasser) Amelia S. Lotz-Havla (Verfasser) Paul Lane (Verfasser) Ignacio Alvarez (Verfasser) Frank Rutsch (Verfasser) SpringerLink (Online service) (Sonstige) |
Published in |
Orphanet journal of rare diseases : OJRD 16, 1, 3.8.2021, date:12.2021, Seite 1-11 |
Published |
2021 |
Language |
|
Country |
|
Topic |
|
Subject |
Medicine/Public Health, general. |
DDC notation |
|
Persistent identifier |
urn:nbn:de:101:1-2021103000305938873308 (URN) |
Record ID |
1244612413 |
Please note
The beta version does not yet contain all functions and information of the DNB portal catalogue. If you are missing information or want to order a medium, please visit the page in the DNB portal catalogue via the following link: