Title |
Stable and durable factor IX levels in patients with hemophilia B over 3 years after etranacogene dezaparvovec gene therapy / Annette von Drygalski, Esteban Gomez, Adam Giermasz, Giancarlo Castaman, Nigel S. Key, Susan U. Lattimore, Frank W. G. Leebeek, Wolfgang Miesbach, Michael Recht, Robert Gut, Ricardo Dolmetsch, Paul E. Monahan, Sandra Le Quellec, Steven W. Pipe |
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Involved |
Annette von Drygalski (Verfasser)
Esteban Gomez (Verfasser) Adam Giermasz (Verfasser) Giancarlo Castaman (Verfasser)
Nigel S. Key (Verfasser)
Susan U. Lattimore (Verfasser) Frank W. G. Leebeek (Verfasser) Wolfgang Miesbach (Verfasser) Michael Recht (Verfasser) Robert Gut (Verfasser) Ricardo Dolmetsch (Verfasser) Paul E. Monahan (Verfasser) Sandra Le Quellec (Verfasser) Steven W. Pipe (Verfasser) |
Published |
Frankfurt am Main: Universitätsbibliothek Johann Christian Senckenberg |
Extent |
Online-Ressource |
Language |
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Country |
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Topic |
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DDC notation |
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Persistent identifier |
urn:nbn:de:hebis:30:3-787765 (URN) |
Further information |
In: Blood advances, 7.2023, 19, S. 5671-5679 |
Record ID |
1350965448 |
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